Reaching for a cure
Pioneering therapeutic interventions for 15q13.3
Reaching out to community
We fund a multi-pronged therapeutic pipeline, from repurposed drugs to pioneering ASO and gene therapies, to address the root genetic causes of the syndrome.
We foster a collaborative ecosystem of patients, families, researchers, and clinicians to align on strategic priorities and provide a trusted source of information.
Drive Broader Impact
Our work provides a direct pathway to understanding and treating more prevalent conditions like autism, schizophrenia, and bipolar disorder.
A Mission Driven by Hope and Scientific Urgency
Tell people about who you are, your origin, your process, or your inspirations. Tap into your creativity. You’ve got this. The way you tell your story online can make all the difference.
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